Phase 2/3 Randomized Trial of Elamipretide in Barth Syndrome, a Genetic Disorder of Cardiolipin Metabolism | RemedyX Labs Research Library
A research summary of A phase 2/3 randomized clinical trial followed by an open-label extension to evaluate the effectiveness of elamipretide in Barth syndrome, a genetic disorder of mitochondrial cardiolipin metabolism, examining phase 2/3 randomized trial of elamipretide in barth syndrome, a genetic disorder of cardiolipin metabolism. Cited source and RUO context from RemedyX Labs.